December 21, 2025
UAE Approves Itvisma Gene Therapy for Spinal Muscular Atrophy, Boosting Patient Hope
The UAE has approved Itvisma (onasemnogene abeparvovec), a gene therapy for spinal muscular atrophy in patients aged two and above. This makes the UAE only the second country to allow this cutting-edge treatment, improving motor functions and offering new hope to patients and families.